Medicine

Accelerating ASO treatments from growth to application

.Completing passions.R.S., M.S., H.G. as well as A.A.R. are actually planners of the 1M1M project. H.G. and also A.A.R. are actually board of supervisors members and also R.S., M.S. as well as A.A.R. are members of the clinical advisory committee of N1C. A.A.R. makes known job by LUMC, which has licenses on exon-skipping technology, some of which has been actually licensed to BioMarin and also subsequently sublicensed to Sarepta. As co-inventor of a few of these patents, A.A.R. was actually entitled to an allotment of royalties. A.A.R. even more divulges acting as impromptu specialist for PTC Therapies, Sarepta Therapeutics, Regenxbio, Dyne Therapies, Lilly, BioMarin Pharmaceuticals Inc., Eisai, Entrada, Takeda, Splicesense, Galapagos, Sapreme, Italfarmaco as well as Astra Zeneca. Before 5 years, A.A.R. additionally did ad hoc consulting with for Alpha Anomeric. A.A.R. also states membership of the clinical advisory boards of Eisai, Hybridize Rehabs, Silence Therapies, Sarepta Therapeutics, Sapreme as well as Mitorx. Over the last 5 years, A.A.R. was likewise a scientific advisory board participant for ProQR. Pay for A.A.R. u00e2 s consulting and also recommending activities is paid out to LUMC. In the past 5 years, LUMC also got audio speaker gratuity coming from PTC Rehabs, Alnylam Netherlands, Italfarmaco as well as Pfizer and funding for arrangement analysis coming from Sapreme, Eisai, Galapagos, Synaffix and also Alpha Anomeric. Venture funding is obtained from Sarepta Therapeutics and Entrada via unlimited gives. H.G. possesses nothing at all to disclose in regard to the subject matters dealt with in this particular document. Before 5 years, he has additionally acquired working as a consultant honoraria coming from UCB. M.S. received consultancy gratuity coming from Ionis, UCB, Prevail, Orphazyme, Biogen, Servier, Reata, GenOrph, AviadoBio, Biohaven, Zevra, Lilly and Solaxa in the past 5 years, all unconnected to the present composition. R.S. possesses nothing to divulge in regard to the subjects dealt with in this particular composition. She has gotten audio speaker and/or working as a consultant gratuity or even funding contributions from Abbvie, Bial, STADA and Everpharma over the last 5 years.